What is the evidence for artesunate for malaria?

Comment by InpharmD Researcher

Available data surrounding the use of artesunate in individuals treated for malaria demonstrate that artesunate has been associated with reduced mortality risk in both adults and children compared to alternative agents (see Tables 1-8). According to CDC guidance, intravenous artesunate is recommended as the first-line treatment for severe malaria in the United States. While several studies suggest artesunate and artemisinin derivatives may be beneficial for other indications (e.g., schistosomiasis), further evaluation is warranted to fully elaborate the therapeutic effect of artesunate in non-malarial diseases.

Background

According to the Expanded Access Investigational New Drug (IND) Protocol for the use of intravenous (IV) artesunate for treating severe malaria in the United States, artesunate is a first-line IV drug for treating severe malaria in the United States. Until stocking of artesunate in pharmacies and hospitals for its immediate use is available, the Centers for Disease Control and Prevention (CDC) will continue to distribute artesunate under its IND protocol for patients in situations where FDA-approved Artesunate for Injection is not yet available ≤ 24 hours of a clinician requesting the drug. To maximize the curative effect of anti-malarial therapy, IV artesunate should be followed by oral treatment with artemether-lumefantrine (Coartem™); atovaquone-proguanil (Malarone); quinine plus either doxycycline or clindamycin; or mefloquine. [1]

Per CDC guidelines for the treatment of malaria, all patients with severe malaria, regardless of infecting species, should be treated with IV artesunate. In cases in which an immediate use of artesunate is unavailable, interim treatment with an effective oral antimalarial should be considered (e.g., artemether-lumefantrine, atovaquone-proguanil, quinine, and mefloquine). If oral intake is restricted, the use of anti-emetics preceding the oral antimalarial or the use of a nasogastric tube for comatose patients may be considered. Upon availability of IV artesunate, immediately discontinue the oral therapy and initiate IV artesunate at a dose of 2.4 mg/kg at 0, 12, and 24 hours. Following the completion of initial IV artesunate therapy, if parasite density is ≤1% and the patient can tolerate oral treatment, a full treatment course with a follow-on regimen must be administered, preferably using artemether-lumefantrine. Other adequate alternatives include atovaquone-proguanil, quinine plus doxycycline or clindamycin, or mefloquine. Mefloquine is reserved for the last due to its severe neuropsychiatric adverse events. [2]

If the patient’s parasite density is >1%, IV artesunate treatment should be continued once a day for an additional 6 days (a maximum of 7 days) until parasite density is ≤1%. A full course of oral follow-on treatment should be initiated as soon as the parasite density ≤1% and the patient can tolerate oral medications. All persons treated for severe malaria with IV artesunate should be monitored weekly for up to four weeks following the treatment initiation for evidence of hemolytic anemia. IV artesunate is considered safe in infants, children, and pregnant women in the second and third trimesters. [2]

The 2023 World Health Organization (WHO) guidelines for malaria recommend treating adults and children with severe malaria (including infants, pregnant women in all trimesters, and lactating women) with IV or intramuscular (IM) artesunate for at least 24 hours and until they can tolerate oral medication. Once a patient has received at least 24 hours of parenteral therapy and can tolerate oral therapy, complete treatment with 3 days of artemisinin-based combination therapy (ACT; strong recommendation; high certainty evidence). Moreover, in both adults and children, parenteral artesunate prevented more deaths than parenteral quinine (high-quality evidence). Artesunate is associated with a small increase in neurological sequelae at the time of hospital discharge (moderate-quality of evidence). The difference is no longer evident on day 28 after discharge (moderate-quality evidence). Parenteral artesunate is recommended as first-line treatment for adults, children, infants, and pregnant women in all trimesters of pregnancy. Although the safety of artesunate in the first trimester of pregnancy has not been firmly established, the proven benefits to the mother outweigh the potential harm to the developing fetus. Furthermore, guidelines strongly recommend that children weighing <20 kg receive a higher dose of artesunate (3 mg/kg body weight per dose) than larger children and adults (2.4 mg/kg per dose) to ensure equivalent exposure to the drug. [3]

A 2012 Cochrane review of the literature analyzed eight randomized controlled trials (RCTs) enrolling 1,664 adults (from 5 studies) and 5,765 children (from 4 studies) to assess the comparative safety and efficacy of artesunate versus quinine for treating severe malaria in patients who were unable to take oral medication. Based on the findings of this review, artesunate significantly reduced mortality risk in both adults (risk ratio [RR] 0.61, 95% confidence interval [CI] 0.50 to 0.75) and children (RR 0.76, 95% CI 0.65 to 0.90). Although artesunate was associated with a transient increase in the incidence of neurological sequelae at hospital discharge in children, no significant differences between treatments were observed in later follow-ups. This review supports the superiority of parenteral artesunate over quinine for treating severe malaria in both adults and children across different regions. However, variations in study design and the need for further research in special populations like pregnant women and repeated dosing may affect generalizability. [4]

A 2017 systematic review included available literature (12 retrospective studies, one prospective study, and seven case reports; N= 624) to assess the efficacy and safety of artesunate in treating severe malaria in travelers and to provide practical implications for its use, with a focus on post-artesunate delayed hemolysis (PADH). With a follow-up duration ranging from 7 days to 6 months, 23 out of 574 patients (4%) with reported outcomes died, but no death was attributed to artesunate toxicity. Non-hematological side effects were uncommon and mild. PADH occurred in 15% of treated patients, with no deaths or sequelae reported. Overall, non-hematological adverse events included mild hepatitis and neurological, renal, cutaneous, and cardiac issues. PADH was the most common hematological side effect, occurring in 15% of patients and requiring blood transfusion in 50% of those cases. Although the lack of prospective randomized controlled trials in travelers limits the generalizability of the findings, this review demonstrated artesunate is highly effective and well-tolerated in travelers with severe malaria. The frequency of PADH necessitates regular hematological follow-up for one-month post-treatment. [5]

A 2004 meta-analysis based on 16 RCTs (N= 5,948; 12 studies in Africa, three in Thailand, and one in Peru; 12 placebo-controlled and double-blinded trials) examined the effects of the addition of artesunate to standard treatment of plasmodium falciparum malaria. The background drugs were chloroquine (three trials), amodiaquine (three), sulfadoxine-pyrimethamine (seven), and mefloquine (three). The study finding showed a significantly lower parasitological failure with 3 days of artesunate at day 14 (OR 0.20, 95% CI 0.17-0.25, n= 4,504) and at day 28 (excluding new infections, 0.23, 0.19-0.28, n= 2,908; including re-infections, 0.30, 0.26-0.35, n= 4,332), as well as a significantly faster parasite clearance (rate ratio 1.98, 95% CI 1.85-2.12, n= 3,517) with artesunate. In subjects with no gametocytes at baseline, artesunate reduced gametocyte count on day 7 (OR 0.11, 95% CI 0.09–0.15, n= 2,734), with larger effects shown on days 14 and 28. Adding artesunate for 1 day (six trials) was associated with fewer failures by day 14 (0.61, 0.48–0.77, n= 1,980) and day 28 (adjusted to exclude new infections 0.68, 0.53– 0.89, n= 1,205; unadjusted including reinfections 0.77, 0.63–0.95, n= 1,958). Potential confounding factors such as age (younger than 10 years, 10 years, and older than 10 years), the intensity of malaria transmission (seasonal or perennial), and packed cell volume did not yield any significant effects on the effect size of artesunate. No significant differences were observed in the occurrence of serious adverse events between artesunate and placebo. Based on these findings, the authors concluded that the addition of 3 days of artesunate to standard antimalarial treatments substantially reduces treatment failure, recrudescence, and gametocyte carriage. [6]

A 2018 review analyzed available data on the use of artesunate and artemisinin derivates in humans for non-malarial indications. A total of 19 studies, including four randomized controlled trials and one meta-analysis, were included for review. Findings indicated that artesunate combined with praziquantel was effective against schistosomiasis (p= 0.003), although artesunate monotherapy was less effective (p<0.001). Additionally, artesunate showed potential as a chemoprophylactic drug against schistosomiasis (p<0.001). Furthermore, while preliminary data suggested possible benefits in treating multidrug-resistant cytomegalovirus infections, the results were largely inconclusive. Moreover, the review did not confirm the efficacy of artesunate and artemisinin derivatives in treating cancers such as cervix, breast, colorectal and lung cancers. Overall, further robust research is necessary to fully understand the therapeutic potential of artesunate in non-malarial diseases and make a definitive conclusion in regards to its place in therapy. [7]

References:

[1] Centers for Disease Control and Prevention (CDC). Expanded access IND protocol: Use of intravenous artesunate for treatment of severe malaria in the United States. Revised February 22, 2021. Accessed March 20, 2025. https://www.cdc.gov/malaria/resources/pdf/Artesunate_Guilin_Protocol_2021.pdf
[2] Centers for Disease Control and Prevention (CDC). Treatment of malaria: Guidelines for clinicians (United States). Reviewed March 27, 2024. Accessed March 20, 2025. https://www.cdc.gov/malaria/hcp/clinical-guidance/treatment-of-severe-malaria.html
[3] World Health Organization (WHO) Guidelines for malaria. Updated March 14, 2023. Accessed March 20, 2025. https://iris.who.int/bitstream/handle/10665/366432/WHO-UCN-GMP-2023.01-eng.pdf?sequence=1
[4] Sinclair D, Donegan S, Isba R, Lalloo DG. Artesunate versus quinine for treating severe malaria. Cochrane Database Syst Rev. 2012;2012(6):CD005967. Published 2012 Jun 13. doi:10.1002/14651858.CD005967.pub4
[5] Roussel C, Caumes E, Thellier M, Ndour PA, Buffet PA, Jauréguiberry S. Artesunate to treat severe malaria in travellers: review of efficacy and safety and practical implications. J Travel Med. 2017;24(2):10.1093/jtm/taw093. doi:10.1093/jtm/taw093
[6] Adjuik M, Babiker A, Garner P, et al. Artesunate combinations for treatment of malaria: meta-analysis. Lancet. 2004;363(9402):9-17. doi: 10.1016/s0140-6736(03)15162-8.
[7] Raffetin A, Bruneel F, Roussel C, et al. Use of artesunate in non-malarial indications. Med Mal Infect. 2018;48(4):238-249. doi:10.1016/j.medmal.2018.01.004

Literature Review

A search of the published medical literature revealed 8 studies investigating the researchable question:

What is the evidence for artesunate for malaria?

Level of evidence

B - One high-quality study or multiple studies with limitations  Read more→



Please see Tables 1-8 for your response.


 

Artesunate Versus Quinine in the Treatment of Severe Falciparum Malaria in African Children (AQUAMAT): An Open-Label, Randomized Trial

Design

Multicenter, open-label, randomized trial 

N= 5,425

Objective

To compare parenteral treatment with either artesunate or quinine in African children with severe malaria.

Study Groups

IV/IM quinine (n= 2,713)

IV/IM artesunate (n= 2,712)

Inclusion Criteria

Children younger than 15 years, a positive rapid diagnostic test for Plasmodium falciparum lactate dehydrogenase and, in the admitting physician's clinical opinion, had severe malaria, and a fully informed written consent from participants' attendant relative or guardian 

Exclusion Criteria

A convincing history of full treatment with parenteral quinine or an artemisinin derivative for more than 24 h before admission

Methods

Eligible patients were randomized to receive the treatment with either IV or IM artesunate or quinine. Artesunate was given in a dose of 2.4 mg/kg on admission, at 12 h, at 24 h, and thereafter once daily until oral medication could be taken reliably. Quinine was given in a 20 mg salt/kg loading dose infused over 4 h (in 5–10 mL/kg of 5% dextrose), followed by a 10 mg salt/kg infusion over 2–8 h three times daily until starting oral therapy. When the patient was able to take tablets, but after a minimum of 24 h of parenteral treatment, oral artemether-lumefantrine in a full standard dose (1.5/9 mg/kg twice daily for 3 days with milk or fat) was given to complete the treatment.

Duration

October 3, 2005, to July 14, 2010

Outcome Measures

Primary: In-hospital mortality

Secondary: Incidence of severe neurological complications, combined outcome measure of death and severe persistent neurological sequelae

Baseline Characteristics

 

IV/IM quinine

(n= 2,713)

IV/IM artesunate

(n= 2, 712)

   

Median age (interquartile range [IQR], years

2.9 (1.7–4.3) 2.8 (1.6–4.2)    

Weight, kg

12.6 ± 4.6 12.4 ± 4.8    

Female

1,295 (48%) 1,315 (48%)     

Median fever before enrolment (IQR), days

3 (2–4) 3 (2–4)     

Median coma before enrolment (IQR), hrs

5.0 (2.5–10)

5.0 (2.0–9.5)

   

Pretreatment with antimalarials

None

Ineffective

Effective

 

1,270 (47%)

371 (14%)

959 (37%)

 

1,281 (47%)

387 (15%)

938 (36%)

   

 Complications on admission

Coma

Convulsions

Severe anemia (hemoglobin <50 g/L)

Severe acidosis (BE <-8 mmol/L)

Severe prostration

Hyperparasitaemia (>10%)

 

945 (35%)

879 (32%)

692 (29%)

975 (43%)

1,668 (61%)

573 (24%) 

 

880 (32%)

811 (30%)

737 (30%)

1,009 (44%)

1,683 (62%)

584 (25%)

   

No major differences in baseline characteristics between the two treatment groups.

Results

Endpoint

IV/IM quinine

IV/IM artesunate

Odds ratio (95% CI)

p-value

In-hospital mortality 

297/2,713 (10.9%) 230/2,712 (8.5%) 0.75 (0.63–0.90) 0.0022

Development of coma

91/1,768 (5.1%) 65/1,832 (3.5%) 0.69 (0.49–0.95) 0.0231

Convulsions developing or persisting >6 h after admission

273/2,713 (10.1%) 224/2,712 (8.3%) 0.80 (0.66–0.97) 0.0199

Deterioration of coma score

208/2,713 (7.7%) 166/2,712 (6.1%) 0·78 (0.64–0.97) 0.0245

Post-treatment hypoglycemia 

75/2713 (2.8%)  48/2,712 (1.8%)  0.63 (0.43–0.91) 0.0134

Adverse Events

No severe adverse effects were attributed directly to drug toxicity.

Study Author Conclusions

Artesunate substantially reduces mortality in African children with severe malaria. These data, together with a meta-analysis of all trials comparing artesunate and quinine, strongly suggest that parenteral artesunate should replace quinine as the treatment of choice for severe falciparum malaria worldwide.

InpharmD Researcher Critique

This relatively robust sample size study showed that parenteral artesunate statistically reduces the overall mortality of African children diagnosed with severe malaria with good tolerability. Though open-label for trial site investigators, other clinical and laboratory investigators were masked to the given parenteral treatments. The similarity of results across the different sites may suggest that significant bias is unlikely.

References:

Dondorp AM, Fanello CI, Hendriksen IC, et al. Artesunate versus quinine in the treatment of severe falciparum malaria in African children (AQUAMAT): an open-label, randomized trial. Lancet. 2010;376(9753):1647-1657. doi: 10.1016/S0140-6736(10)61924-1.

 

Artesunate Versus Quinine for Treatment of Severe Falciparum Malaria: A Randomised Trial (SEAQUAMAT Study)

Design

Multicentre, open-label, randomized controlled trial

N= 1,461

Objective

To establish conclusively which, of intravenous (IV) artesunate or IV quinine, is the more effective drug for the treatment of severe malaria

Study Groups

IV Artesunate (n= 730)

IV Quinine (n= 731)

Inclusion Criteria

Patients aged >2 years with a positive blood antigen stick test for Plasmodium falciparum histidine-rich protein 2 (HRP2); diagnosis of severe malaria, according to the admitting physician

Exclusion Criteria

A convincing history of full treatment with quinine (40 mg/kg on the first day and 30 mg/kg on any subsequent day) or an artemisinin derivative for more than 24 h before admission, or if known allergy to one of the artemisinin derivatives or quinine

Methods

Eligible patients were randomized to receive either IV artesunate 2.4 mg/kg body weight given as a bolus at 0, 12, and 24 h, and then daily until oral medication could be taken reliably, or IV quinine (20 mg salt/kg loading dose infused over 4 h then 10 mg/kg infused over 2–8 h three times a day). The participating centers were located in Bangladesh, Myanmar (Burma), India, and Indonesia

When the IV artesunate patient had recovered sufficiently to take tablets, oral artesunate 2 mg salt/kg/day was given to complete a total course (including parenteral treatment) of 7 days of artesunate, providing a total cumulative dose of 17–18 mg/kg. Alternatively, IV quinine patient was administered oral quinine 10 mg/kg every 8 h to provide a total quinine course of 7 days. Some hospitals combined both regimens with oral doxycycline 100 mg twice a day for 7 days once the patient could take oral medication. 

Duration

June 2003, to May 2005

Outcome Measures

Primary: Death from severe malaria

Secondary: Incidence of neurological sequelae, combined death or neurological sequelae, recovery times (times to discharge), and development of severe complications

Baseline Characteristics

 

IV Artesunate

(n= 730)

IV Quinine

(n= 731)

   

Mean age, years

27.9  27.9     

Child (age <15 years)

97 (13%) 105 (14%)     

Male

546 (75%) 529 (72%)     

Pregnant 

23 of 133 (17%) 26 of 143 (18%)    

Pretreatment with antimalarial drug

167 (23%) 142 (19%)    

Severe malaria

509 (70%) 541 (74%)    

Malaria parasites on blood film

708 (97%) 716 (98%)    

Hyperparasitaemia (>10%)

121 (17%) 108 (15%)    

Complications on admission

Coma*

Jaundice (clinical)

Acidosis (base excess less than –3.3 mmol/L)

Convulsion

Shock (clinical)

Respiratory distress

History of anuria

 

284 (39%)

355 (49%)

308/662 (47%)

89 (12%)

78 (11%)

79 (11%)

99 (14%)

 

304 (42%)

349 (48%)

334/648 (52%)

87 (12%)

92 (13%)

96 (13%)

135 (18%)

   

*Glasgow coma scale <11 or Blantyre coma scale <3

Results

Endpoint

IV Artesunate 

(n= 730)

IV Quinine

(n= 731)

Mantel-Haenszel stratified OR/hazard ratio [HR] (95% confidence interval [CI])

p-value

In-hospital death

107 (15%) 164 (22%) 0.60 (0.45–0.79) 0.0002

Death within 48 h of entry

61 (8%) 75 (10%) 0.81 (0.57–1.16) 0.25

Death after 48 h of entry

46 (6%) 89 (12%)

0.48 (0.33–0.70)

0.0001

In-hospital death (blood-smear positive)

105 of 689 (15%) 157 of 693 (23%) 0.62 (0.47–0.82) 0.0007

Neurological sequelae

7 (1%) 3 (<1%) 2.3 (0.59–8.8) 0.22

Combined outcome: in-hospital death or neurological sequelae

114 (16%) 167 (23%) 0.63 (0.48–0.82) 0.0007

Fetal death

5 of 23 (22%) 5 of 26 (19%) 1·33 (0.28–6.18) 0.72

Time to discharge, days; median (IQR, range)

5 (4–8, 0–54) 5 (4–8, 0–45) hr 0.93 (0.83–1.04) 0.20

Development of severe complications

Convulsions after entry

Shock developing after entry

Hypoglycemia after entry

Blackwater fever after entry

Dialysis after entry

Vasopressor treatment after entry

Mechanical ventilation after entry 

 

31 (4%)

26 (4%)

6 (<1%)

49 (7%)

60 (8%)

23 (3%)

26 (4%)

 

43 (6%)

36 (5%)

19 (3%)

33 (5%)

48 (7%)

24 (3%)

39 (5%)

 

0.70 (0.44–1.12)

0.72 (0.43–1.21)

0.31 (0.12–0.78)

1.58 (0.94–2.65)

1.25 (0.85–1.85)

0.92 (0.52–1.64)

0.65 (0.39–1.1)

 

0.14

0.22

0.009

0.08

0.25

0.78

0.11

Study Author Conclusions

Artesunate should become the treatment of choice for severe falciparum malaria in adults.

InpharmD Researcher Critique

Despite considerable differences in the intensive-care support among trial sites, a large reduction in mortality was consistent throughout. Given that the trial was mainly conducted in adults in areas of low and unstable transmission, the study findings cannot be extrapolated to the treatment of severe malaria in children in areas of higher transmission. 

References:

Dondorp A, Nosten F, Stepniewska K, et al. Artesunate versus quinine for treatment of severe falciparum malaria: a randomised trial. Lancet. 2005;366(9487):717-725. doi: 10.1016/S0140-6736(05)67176-0.

 

Cost-Effectiveness of Artesunate for the Treatment of Severe Malaria

Design

Cost-effectiveness analysis

N= 1,461

Objective

To explore the cost‐effectiveness of artesunate against quinine based principally on the findings of a large multi-center trial (SEAQUAMAT study) carried out in Southeast Asia.

Study Groups

One site each in Bangladesh, India, Indonesia and seven sites in Myanmar

Inclusion Criteria

SEAQUAMAT study: Patients' age >2 years with a positive blood antigen stick test for Plasmodium falciparum histidine-rich protein 2 (HRP2), and a diagnosis of severe malaria according to the admitting physician

Exclusion Criteria

SEAQUAMAT study: A convincing history of full treatment with quinine (40 mg/kg on the first day and 30 mg/kg on any subsequent day) or an artemisinin derivative for more than 24 h before admission, or if known allergy to one of the artemisinin derivatives or quinine

Methods

Trial data were used to compare mortality of patients with severe malaria, treated with either artesunate or quinine. This was combined with retrospectively collected cost data to estimate the incremental cost per death averted with the use of artesunate instead of quinine.

Costs were converted from local units to US dollars at the relevant year, adjusted for inflation using the consumer price index, and reported in 2008 USD.

Duration

SEAQUAMAT study: between 2003 and 2005.

Outcome Measures

Incremental cost per death averted using artesunate.

Baseline Characteristics

One site each in Bangladesh, India, Indonesia and seven sites in Myanmar.

Results

Endpoint

Bangladesh

India

Indonesia

Myanmar

Pooled

Mean cost for patients treated with quinine

$26.8 $51.1 $54.8 $17.5 $32.4

Mean cost for patients treated with artesunate

$42.8 $68.9 $66.0  $25.8 $43.0

Relative risk for treatment with artesunate

0.72 0.81 0.51 0.57 0.65

Numbers needed to treat to avert a death

11 20 17 13 13

Incremental cost per death averted

$177.2 $358.9 $185.7 $104.8 $135.6

By removing the highest and lowest 2.5% of observations, a 95% interval was created, ranging from −$120 to $455. The negative values indicate those instances where artesunate is more effective and less costly.

Study Author Conclusions

This analysis confirms the vast superiority of artesunate for the treatment of severe malaria from an economic as well as a clinical perspective.

InpharmD Researcher Critique

Though this analysis provides some economic perspective, this is solely based on one study. Pooling cost data raises concerns around how prices are standardized, as the unit costs can vary widely across countries. 

References:

Lubell Y, Yeung S, Dondorp AM, et al. Cost-effectiveness of artesunate for the treatment of severe malaria. Trop Med Int Health. 2009;14(3):332-337. doi: 10.1111/j.1365-3156.2009.02227.x.

 

Intramuscular Artesunate for Severe Malaria in African Children: A Multicenter Randomized Controlled Trial

Design

Open-label, randomized, multicenter, parallel-group, three-arm, non-inferiority study

N= 1,047

Objective

To compare the efficacy and safety of a simplified three-dose intramuscular (IM) or intravenous (IV) artesunate regimen with the standard WHO-recommended five-dose regimen in children with severe malaria, using a non-inferiority design

Study Groups

Three-Dose IV (n= 351)

Three-Dose IM (n= 348)

Five-Dose IM (n= 348)

Inclusion Criteria

Children aged 0.5 to 10 years with severe malaria; specific inclusion criteria detailing the definition of severe malaria, any laboratory values, or clinical conditions required for inclusion were not specified

Exclusion Criteria

Not specified

Methods

Patients were treated with parenteral artesunate regimen at differing doses and intervals depending on their group allocation. Artemether-lumefantrine was administered at discharge, and standard malaria treatment protocols were followed. Population pharmacokinetic studies were performed on a subset of patients.

Children were randomized (1:1:1) to receive one of three treatment regimens: a control regimen of five IM injections of artesunate regimen at a total dose of 12 mg/kg (2.4 mg/kg at 0, 12, 24, 48, and 72 hours), or a simplified regimen of three IM or IV injections of 4 mg/kg (at 0, 24, and 48 hours).

Duration

Recruitment: July 4, 2011 until September 25, 2012

Follow-up: at least 28 days following the first dose 

Outcome Measures

Primary: Proportion of children with ≥ 99% reduction in parasitemia at 24 hours from admission

Baseline Characteristics

 

Three-Dose IV (n= 351)

Three-Dose IM (n= 348)

Five-Dose IM (n= 348)

Age, years

4.0 ± 2.4 4.1 ± 2.5 4.2 ± 2.5

Female

46% 48% 48%

Laboratory findings (range), mean

Parasitemia per microliter × 10−3

Hemoglobin, g/dl

 

129.0 (4.6 to 2,965.0) 

8.5 ± 2.4

 

114.0 (5.0 to 1,439.0)

8.7 ± 2.3

 

119.0 (4.1 to 2,675.0)

8.7 ± 2.4

Clinical signs of severe malaria

Severe anemia

Hyperlactatemia

Hyperparasitemia

Hypoglycemia

Jaundice

 

34 (10%) 

21 (6%) 

103 (29%) 

13 (4%) 

28 (8%) 

 

42 (12%) 

18 (5%) 

91 (26%) 

7 (2%) 

29 (8%) 

 

40 (11%) 

23 (7%)

103 (30%)

18 (5%)

25 (7%)

Results

Rate of ≥ 99% reduction in parasitemia at 24 hours:

Three-dose IM arm, 265/338 (78%) vs. five-dose IM regimen, 263/331 (79%): demonstrating non-inferiority of the simplified three-dose regimen to the conventional five-dose regimen (95% confidence interval −7 to 5; p= 0.02)

In three-dose IV arm, 246/333 (74%) vs. children had ≥ 99% reduction in parasitemia at 24 h (non-inferiority of this regimen to the five-dose control regimen was not shown (p= 0.24).

Adverse events

In a post hoc analysis, 192/885 (22%) of children developed delayed anemia, an adverse event associated with increased leukocyte counts. There was no observed difference in delayed anemia between treatment arms.

Study Author Conclusions

A simplified three-dose IM regimen for severe malaria in African children is non-inferior to the more complex WHO-recommended regimen. Parenteral artesunate is associated with a risk of delayed anemia in African children.

InpharmD Researcher Critique

Although the primary outcome measures were assessed in a blinded manner, the results are subject to potential biases owing to the open-label design and the high rates of participant loss to follow-up.



References:

Kremsner PG, Adegnika AA, Hounkpatin AB, et al. Intramuscular Artesunate for Severe Malaria in African Children: A Multicenter Randomized Controlled Trial. PLoS Med. 2016;13(1):e1001938. Published 2016 Jan 12. doi:10.1371/journal.pmed.1001938

Randomized controlled trial of artesunate or artemether in Vietnamese adults with severe falciparum malaria

Design

Single-center, randomized, double-blind trial

N= 370

Objective

To compare the efficacy and safety of intramuscular (IM) artesunate versus IM artemether in treating severe falciparum malaria in Vietnamese adults

Study Groups

IM artesunate (n= 186)

IM artemether (n= 184)

Inclusion Criteria

Patients with peripheral-blood smears showing asexual forms of Plasmodium falciparum and at least one severe malaria complication such as cerebral malaria, renal acute failure, jaundice with specific parameters, hypoglycemia, anemia, hyperparasitemia, hyperlactatemia, metabolic acidosis, or shock

Exclusion Criteria

Patients aged<14 years, pregnant in the first trimester, known intravenous drug abusers, those who received more than 3 g of quinine or 2 doses of artemisinin derivatives within 48 hours before admission, history of allergy to artemisinin derivatives, or known to be HIV positive

Methods

Patients were randomized to receive either intramuscular artesunate (2.4 mg/kg immediately followed by 1.2 mg/kg at 12 hours then 24 hours then daily) or artemether (3.6 mg/kg immediately followed by 1.8 mg/kg daily) following specific dosage regimens for a minimum of 72 hours for both drugs. 

Both drugs were given IM until oral medication could be taken reliably. Oral artesunate was given 2 mg/kg/day to complete a 7 day treatment course, including parenteral doses, providing a total cumulative dose between 17 and 18 mg/kg over 7 days. If parasitemia did not fall by >75% within 48 hours from admission and intravenous quinine (20 mg/kg followed by 10 mg/kg every 8 hours) was given, the treatment was considered a failure. 

Duration

May 1996 to June 2003

Outcome Measures

Mortality rate, parasite clearance time, adverse events, and various clinical and laboratory markers of recovery from severe malaria

Baseline Characteristics

Both groups were comparable in terms of age, sex, previous treatment, Glasgow Coma Score, presence of shock, hypoglycemia, hematocrit, parasite and white cell counts, and other biochemistry markers.

Results

Mortality was lower in the artesunate group (7%) compared to the artemether group (13%); unadjusted relative risk of death for artesunate 0.54 (95% confidence interval [CI], 0.28 to 1.02; p= 0.052).

Parasitaemia declined more rapidly in the artesunate group. Overall, both treatments were well tolerated with no significant differences in adverse events. No significant differences in hematologic recovery or blood transfusion requirements were seen between groups. 

Adverse Events

Adverse events were similar between the groups, with low rates of hypoglycemia (7% vs. 9%) and no severe unexpected events.

Study Author Conclusions

Intramuscular artesunate may be superior to intramuscular artemether for treating severe malaria in adults.

Critique

The study indicates a potentially better efficacy and faster parasite clearance with artesunate. However, early termination of the study due to declining patient numbers limits the statistical power. Future research should ideally further explore these findings with a larger sample size and in different demographic settings.

References:

Phu NH, Tuan PQ, Day N, et al. Randomized controlled trial of artesunate or artemether in Vietnamese adults with severe falciparum malaria. Malar J. 2010;9:97. Published 2010 Apr 15. doi:10.1186/1475-2875-9-97

A Randomized Controlled Trial of Artemether-Lumefantrine Versus Artesunate for Uncomplicated Plasmodium falciparum Treatment in Pregnancy

Design

Open-label, randomized, comparative, controlled trial 

N= 253

Objective

To assess the efficacy, tolerability, and safety of artemether-lumefantrine compared to artesunate for uncomplicated Plasmodium falciparum malaria in pregnancy

Study groups

Artemether-lumefantrine (n= 125)

Artesunate (n= 128)

Inclusion criteria

Pregnant women in second or third trimester with uncomplicated malaria
Exclusion criteria

Women with chronic disease, splenectomy, severe malaria, imminent delivery, or intolerance to medications; initial restriction to a second malaria episode in pregnancy was later expanded

Methods

Patients were randomized to receive directly observed treatment with either three day artemether-lumefantrine (20/120 mg artemether/lumefantrine) four tablets twice a day for 3 days, with 250 mL of chocolate milk containing 7 g of fat at each dose (given at 0, 8, 24, 36, 48 and 60 h), or artesunate 2 mg/kg (50 mg tablets) once daily for seven days.

Participants received directly observed therapy and were followed up weekly until delivery or day 42; blood samples were taken, and newborns were assessed at birth and one year.

Duration

Enrollment: April 23, 2004 to August 29, 2006

Follow-up: until 42 days or delivery, whichever was later

Outcome measures

Primary: P. falciparum PCR-adjusted cure rates

Secondary: adverse events, birth outcomes, infant health, and developmental metrics up to 1 year

Baseline characteristics

No significant differences; the average gestational age was 24 weeks, and similar parasitemia, anemia prevalence, and malaria history

Results

 

The cure rates (95% confidence interval [CI]):

Intention to treat (ITT) population: artesunate monotherapy, 89.2% (95% CI 82.3% to 96.1%) vs. artemether-lumefantrine, 82.0% (95% CI 74.8% to 89.3%); p= 0.054

Per protocol (PP): AS7 89.7% (95% CI 82.6% to 96.8%) vs. AL 81.2% (95% CI 73.6% to 88.8%); p= 0.031

One-third of the PCR-confirmed recrudescent cases occurred after 42 days of follow-up.

Birth outcomes and infant (up to age one year) outcomes did not differ significantly between the two groups.

Adverse events

Generally well tolerated; one drug-related serious adverse event; some minor side effects, no significant difference between treatment groups.

Conclusions

Artemether-lumefantrine was safe but less efficacious than artesunate in pregnancy; higher doses or longer regimens may be needed; efficacy assessment requires extended follow-up to capture delayed recrudescences.

Critique

Despite the comprehensive follow-up, the results are limited by open-label design, smaller samples for some sub-analyses, and lack of blinding.
References:

McGready R, Tan SO, Ashley EA, et al. A randomized controlled trial of artemether-lumefantrine versus artesunate for uncomplicated plasmodium falciparum treatment in pregnancy. PLoS Med. 2008;5(12):e253. doi:10.1371/journal.pmed.0050253

Intravenous Artesunate for the Treatment of Severe Imported Malaria: Implementation, Efficacy, and Safety in 1,391 Patients

Design

Prospective observational study

N= 1,391

Objective To assess the implementation, efficacy, and safety of intravenous (IV) artesunate in treating severe imported malaria in a real-world setting in France
Study Groups

IV artesunate (n= 1,391)

Inclusion Criteria

Patients treated with IV artesunate at any of the 110 network sites in France during the study period 

Exclusion Criteria

No specific exclusion criteria were mentioned; the study included all artesunate-treated patients irrespective of their clinical status or underlying conditions

Methods

Data was collected from the Malaria National Reference Center database, medical charts, and specific distribution program forms. Adverse events were also obtained from a national pharmacovigilance system. Statistical analyses were performed to compare different subgroups.

Different subgroups were analyzed, including those based on geographic origin, age, pregnancy status, immunocompromised status, and initial parasitemia levels.

Duration May 25, 2011 to December 31, 2017
Outcome Measures

Primary: overall mortality and incidence of adverse events (AEs)

Secondary: length of hospital and ICU stays, parasite clearance rates, and instances of post-artesunate-delayed hemolysis (PADH)

Baseline Characteristics

Out of 1,391 patients, the majority were from Africa (67.7%), men (65.9%), and 74.6% lived in non-endemic areas. Age distribution varied with patients under 15 making up 9.2% and over 65 making up 8.9%.

Results

Artesunate significantly increased in use from 9.9% in 2011 to 71.4% in 2017. No outcome differences were observed between the patients with initial parasitemia < 4% and those with initial parasitemia from 4% to 10%.

The overall mortality was 4.1%, with severe cases showing lower lethality over time.

PADH incidence was high at 42.8% in a specific assessment subgroup. At the end of follow-up, sequelae were reported in 8.4% of patients (48 out of 574 patients).

Adverse Events AEs were reported in 42.4% of patients with anemia and hemolysis being the most frequent. Other AEs included cardiac events (4.2% including conduction disorders/arrhythmias), and liver enzyme elevations (3.6%). No fatal outcomes were attributable directly to artesunate.
Study Author Conclusions Intravenous artesunate was rapidly and effectively deployed nationwide, showing robust clinical benefits and manageable safety profiles. Although PADH was frequent, it did not result in fatal outcomes. Further research should focus on rare cardiac AEs and outcomes during the first trimester of pregnancy.
Critique The study provides valuable real-world insights but involves inherent limitations of biases owing to its observational nature. Some minor AEs might be underreported, and causality for AEs cannot be definitively established. The high frequency of PADH needs standardized monitoring using predictive tests, especially among non-immune travelers.
References:

Roussel C, Ndour PA, Kendjo E, et al. Intravenous Artesunate for the Treatment of Severe Imported Malaria: Implementation, Efficacy, and Safety in 1391 Patients. Clin Infect Dis. 2021;73(10):1795-1804. doi:10.1093/cid/ciab133

 

Intravenous Artesunate for the Treatment of Severe and Complicated Malaria in the United States: Clinical Use Under an Investigational New Drug Protocol

Design

Retrospective case series

N= 102

Objective

To assess the safety and clinical benefit of intravenous (IV) artesunate as a quinidine alternative

Study Groups

IV artesunate (n= 102)

Inclusion Criteria

Must have met at least one criterion in each of 3 groups of enrollment criteria, designated A, B and C.

Group A Criteria: Microscopic confirmation of malaria or a strong clinical suspicion of severe malaria when microscopic diagnosis was unavailable.

Group B Criteria: Patient’s need for IV treatment due to one or more of the following: inability to tolerate oral medications; high density parasitemia (≥5%); or evidence of severe malaria [impaired consciousness; seizures; circulatory collapse/shock; pulmonary edema or ARDS; acidosis; acute renal failure; abnormal bleeding or disseminated intravascular coagulation (DIC); jaundice; or severe anemia with hemoglobin < 7 g/dL)].

Group C Criteria: Patient’s need for artesunate due to at least one of the following factors: problems with quinidine availability; failure (parasitemia >10% of baseline value at 48 hours after starting IV quinidine); intolerance; or contraindications.

Exclusion Criteria

A known allergy to artesunate

Methods

Clinical and laboratory data from each eligible patient’s hospital records were abstracted retrospectively. Eligible patients received IV artesunate 2.4 mg/kg body weight given as a bolus at 0, 12, and 24 h, 48 h then follow-on oral antimalarial therapy after a minimum of 4-hour waiting period. 

Duration

January 2007 through December 2010

Follow-up period: 7 days

Outcome Measures

Primary: Mortality

Secondary: Time to negative parasitemia, time to follow-on oral therapy, time to discharge from the ICU, and change in enrollment B Criteria vs. baseline

Baseline Characteristics

 

IV artesunate

(n= 102)

Age, years

38.1 (range, 1-72 years)

Adults (age ≥15) 

Children

92

10

Male

62 (61%) 

Ethnicity

White

Black/African Americans

Asians

Undisclosed

 

26 (25%)

64 (63%)

9 (9%)

3 (3%) 

Malaria was confirmed by microscopy

96%

Mean baseline parasitemia

13.8% 

Baseline clinical status

Severe or life-threatening renal impairment

Severe or life-threatening liver impairment

baseline markers for cerebral malaria

 

14% 

17%

35%

Reason for requiring parenteral treatment

Parasitemia ≥5% 

Jaundice

Inability to take oral medications

 

66%

47%

35% 

Results

Endpoint

IV artesunate

(n= 102)

Mortality 

6.9%

Median time to negative parasitology, hrs

42.7 

Median time to discharge from the Intensive Care Unit, days

All deaths and most adverse events were attributed to the severity of malaria. Patients’ symptoms generally improved or resolved within 3 days. Over 100 concomitant medications were used, with no documented drug-drug interactions.

Adverse Events

Common Adverse Events: Anemia (65%), increased hepatic transaminases (49%), thrombocytopenia (18%), hyperbilirubinemia (14%), acute renal failure (10%), ARDS (8%). 

Serious Adverse Events: 20% Grade 4 AE (13 reports of anemia, 9 reports of respiratory failure/collapse/ARDS)

Study Author Conclusions

IV artesunate was safe and clinically beneficial in the vast majority of US patients who were treated with the drug during the targeted period, thus supporting the use of artesunate as a quinidine alternative.

InpharmD Researcher Critique

 

The study is subject to the limitations inherent to a retrospective analysis. However, the study is focused on the U.S. population which is considered a major strength of this study. Given that the study has a short follow-up period of 7 days, there are potential late-presenting safety issues. 

Seven deaths are attributed to the severity of malaria (e.g., cerebral malaria and moderate-severe hepatic injury at baseline) rather than to artesunate.

References:

Twomey PS, Smith BL, McDermott C, et al. Intravenous artesunate for the treatment of severe and complicated malaria in the United States: Clinical use under an investigational new drug protocol. Ann Intern Med. 2015;163(7):498-506. doi:10.7326/M15-0910.