What evidence is there to support AUC:MIC dosing of vancomycin for CNS infections?

Comment by InpharmD Researcher

Current evidence and guideline recommendations for vancomycin therapeutic drug monitoring have shifted from traditional peak/trough-based dose adjustments toward area under the curve (AUC)-guided dosing strategies to optimize efficacy while reducing nephrotoxicity risk. Although trough concentrations were previously targeted at 15 to 20 mg/L for serious methicillin-resistant Staphyloccous aureus (MRSA) infections, updated consensus guidelines no longer recommend trough-only monitoring because higher troughs may increase acute kidney injury without clear additional benefit. Current recommendations support targeting an individualized AUC/MIC ratio of 400 to 600 mg*h/L, with Bayesian-guided dosing preferred when available, as multiple studies and meta-analyses have demonstrated lower nephrotoxicity rates with AUC-guided monitoring compared with trough-guided approaches while maintaining similar clinical outcomes. Specifically for central nervous system (CNS) infection, available evidence is limited but shows that use of AUC/MIC dosing at CNS weight-based dosing frequencies targeting the recommended 400 to 600 mg*h/L range for systemic infections yields AUCs within the goal range and appears promising, and that a therapeutic target at the upper end of the recommended AUC range is likely more suitable for MRSA CNS infections.
Background

The revised consensus guidelines on therapeutic monitoring of vancomycin for serious methicillin-resistant Staphylococcus aureus (MRSA) infections from the American Society of Health-System Pharmacists (ASHP), the Infectious Diseases Society of America (IDSA), the Pediatric Infectious Diseases Society (PIDS), and the Society of Infectious Diseases Pharmacists (SIDP) were published to provide updated recommendations in regards to specific dosing and monitoring of vancomycin, which was not reflected in the original consensus guidelines published in 2009. Trough-only monitoring, with a target of 15 to 20 mg/L, is no longer recommended based on efficacy and nephrotoxicity data in patients with serious infections due to MRSA. Given the narrow vancomycin area under the curve (AUC) range for therapeutic effect and minimal acute kidney injury (AKI) risk, it is now recommended that the most accurate and optimal way to manage vancomycin dosing is through AUC-guided dosing and monitoring. [1], [2]

To accomplish this, the guidelines recommend two approaches, one of which relies on the collection of 2 concentrations (obtained near steady-state, post-distributional peak concentration [Cmax] at 1 to 2 hours after infusion and trough concentration [Cmin] at the end of the dosing interval), preferably but not required during the same dosing interval (if possible) and utilizing first order pharmacokinetic (PK) equations to estimate the AUC. The preferred approach to monitor AUC, however, involves the use of Bayesian software programs, embedded with a PK model based on richly sampled vancomycin data as the Bayesian prior, to optimize the delivery of vancomycin based on the collection of 1 or 2 vancomycin concentrations, with at least 1 PK sample representing a trough. With this approach, it is preferred to obtain 2 PK samples (i.e., at 1 to 2 hours post-infusion and at the end of the dosing interval) to estimate the AUC. A trough concentration alone may be sufficient to estimate the AUC with the Bayesian approach in some patients, but more data are needed across different patient populations to confirm the viability of using trough-only data. [1]

For patients with suspected or definitive serious MRSA infections, an individualized target of AUC over 24 hours to minimum inhibitory concentration (MIC) determined by broth microdilution (AUC/MICBMD) ratio of 400 to 600 mg*h/L (assuming a vancomycin MICBMD of 1 mg/L) should be advocated to achieve clinical efficacy while improving patient safety. Doses of 15 to 20 mg/kg (based on actual body weight) administered every 8 to 12 hours as an intermittent infusion are recommended for most patients with normal renal function when assuming a MICBMD of 1 mg/L. In patients with normal renal function, such doses may not achieve the therapeutic AUC/MIC target when the MIC is ≥2 mg/L. It should be noted that there is insufficient evidence to provide recommendations on whether trough-only or AUC-guided vancomycin monitoring should be used among patients with noninvasive MRSA or other infections. [1]

A 2021 review discusses the most substantial changes in the revised 2020 vancomycin consensus guidelines including the recommendation to transition from trough-only to AUC-guided dosing and monitoring for patients receiving vancomycin for “suspected or definitive serious invasive MRSA infections” and to maintain daily AUCs between 400 to 600 mg*h/L. In general, the basis for the shift from troughs of 15-20 mg/L to AUC-guided dosing and monitoring was to minimize vancomycin-associated acute kidney injury (VA-AKI) while maintaining similar effectiveness. Available data indicate that VA-AKI increases as a function of the intensity and duration of vancomycin exposure. Despite being widely utilized in practice, data demonstrating the clinical benefits of maintaining higher troughs are lacking. The 2009 consensus guidelines recommended maintaining troughs between 15 and 20 mg/L to simplify dosing and monitoring, but there were a lack of high-quality efficacy and safety data to support this recommendation at the time, and it was solely based on the fact that a trough within this range will consistently ensure a daily AUC greater than 400 mg*h/L. Despite this, the 2009 consensus guidelines did not account for the fact that a wide range of upper AUC values can occur with any given trough value. When examining the relationship between day 2 trough and AUC among simulated subjects with troughs between 15 and 20 mg/L, 48% of patients will have daily AUCs greater than 600 mg*h/L, which could result in a higher risk for VA-AKI. [1], [2], [3]

The AUC can be estimated with limited PK sampling in real time with either Bayesian software programs or simple analytic PK equations, but the former is suggested to be the preferred approach for precision dosing for desired AUCs. As Bayesian programs are flexible and adaptable, vancomycin concentrations can be obtained at any time, even over different dosing intervals; vancomycin concentrations do not need to be collected at “steady state” conditions. Additionally, the Bayesian approach provides the ability to include covariates, such as creatinine clearance, in the structural PK models to provide optimal dosing in patients with fluctuating renal function. [3]

There are now data indicating that AUC-guided dosing relative to trough-based monitoring is associated with less VA-AKI and comparable outcomes. In a retrospective, quasi-experimental study of 1,280 hospitalized patients (Table 1), AUC-guided dosing was found to be independently associated with a significant decrease in AKI (odds ratio [OR] 0.52, 95% confidence interval [CI] 0.34 to 0.80). In a prospective National Institutes of Health-funded study (Table 2), patients were monitored via troughs (range of 10 to 20 mg/L) in year 1 versus estimated Bayesian AUCs of ≥400 mg*h/L in years 2 and 3. Nephrotoxicity occurred in 8% of subjects in year 1 compared with 0% and 2% of subjects in years 2 and 3 (p= 0.01). Additionally, there was no difference in efficacy between the approaches. Overall, the authors suggest that having a landmark double-blind, well-powered randomized controlled trial (RCT) would be ideal to drive recent recommendations. However, an RCT of this nature is unlikely given that vancomycin has been in existence for over 50 years and there has yet to be one RCT published to define optimal monitoring practices. [3], [4], [5]

A 2023 systematic review and meta-analysis evaluated vancomycin-associated nephrotoxicity associated with AUC-guided versus trough-guided dosing. The analysis was conducted based on data from 57 studies, encompassing mostly adult and elderly patients. Of these, 4 studies directly compared AUC-guided versus trough-guided monitoring, with pooled results finding a significantly lower incidence of nephrotoxicity in the AUC-guided group (OR 0.53; 95% CI 0.32 to 0.89; p= 0.02; I2= 45%). The risk of nephrotoxicity was unaffected by the AUC derivation method. AUC thresholds correlated with nephrotoxicity only within the first 96 hours of therapy. Some individual studies reported the AUC-guided group to have statistically lower vancomycin cumulative and maintenance doses along with decreased overall drug exposure in comparison to the trough-guided group. A multivariate analysis (n= 38 studies) found concurrent nephrotoxins (68.4%), higher vancomycin trough concentrations (68.4%), and vancomycin duration of use (31.6%) to be predictors of nephrotoxicity. These results support conclusions made by other available studies, suggesting AUC-guided monitoring is associated with lower risk of vancomycin-related nephrotoxicity compared to trough-guided monitoring. In addition to heterogeneity, possibly related to varying definitions and durations of monitoring, the overall patient sample included mostly adult and older adult patients, hindering generalizability to other patient groups. [6]

A 2022 systematic review synthesized findings from 19 clinical investigations, comprising a total of 482 patients, to evaluate the efficacy, safety, and pharmacokinetics of both intravenous (IV) and intraventricular (IVT) vancomycin in the treatment of central nervous system (CNS) infections, including meningitis, ventriculitis, and CNS device-associated infections. The review highlighted that the optimal dosing regimens still remain unclear, and therapeutic drug monitoring (TDM) is often conducted to ensure adequate cerebrospinal fluid (CSF) concentrations. Across the included studies, IV vancomycin doses ranged from 1,000 to 3,000 mg/day, with dosing frequencies commonly at 15 mg/kg every 6 hours. IVT vancomycin doses spanned from 2 to 20 mg/day, typically administered once daily. TDM was conducted in 14 of the reviewed studies, although no consistent relationship was found between CSF vancomycin concentrations and therapeutic efficacy or toxicity. Pharmacokinetic data revealed wide variability in CSF concentrations for both IV (0.06 to 22.3 mg/L) and IVT (2.5 to 292.9 mg/L) administration routes. Notably, CSF-to-serum ratios varied significantly, ranging from 0.00 to 0.81 mg/L, with some studies suggesting enhanced penetration in the presence of meningeal inflammation. No clear relationships were found between vancomycin CSF levels and efficacy or toxicity. No serious adverse effects, including nephrotoxicity, were attributed to either IV or IVT vancomycin administration. Clinical outcomes indicated favorable responses in most cases, with CSF sterilization achieved in 88.4% of patients treated with IVT vancomycin alone. Despite observed efficacy and an acceptable safety profile, the review highlighted the need for high-quality clinical trials to further delineate optimal dosing strategies and characterize CNS pharmacokinetics to inform therapeutic decision-making in CNS infections. [7]

A 2021 systematic review and meta-analysis evaluating the relationship between vancomycin monitoring strategies and vancomycin effectiveness and safety included subjects who had MRSA bacteremia only for analysis of the effectiveness. As considerable variation in the AUC/MIC ratio was noted across included studies likely due to differences in methodological and technical measurements, researchers rounded the AUC within 15%. As such, the cut-off value of AUC/MIC ratios of 340-460 mg*h/L was defined as 400 mg*h/L, and AUC values of 510-690 mg*h/L were defined as 600mg*h/L. Pooled meta-analysis of effectiveness and safety each contained five studies, primarily retrospective in design. Results found individuals with vancomycin trough concentrations ≥15 mcg/mL had significantly lower treatment failure rates (OR 0.63, 95% CI 0.47 to 0.85). Compared to those with a trough of 15 to 20 mcg/mL, adult patients with a trough concentration ≥20 mcg/mL had a significantly higher risk of developing acute kidney injury (AKI) (OR 2.39; 95% CI 1.78 to 3.20). The analysis of target AUC/MIC found high AUC/MIC level (cut-off 400 mg*h/L ± 15%) to be associated with significantly lower treatment failure rates (OR 0.28; 95% CI 0.18 to 0.45), whereas a level of 600 mg*h/L ± 15% significantly increased the risk of AKI (OR 2.10; 95% CI 1.13 to 3.89). Overall, the pooled analysis did not report significant differences in the incidence of AKI and mortality between AUC-guided monitoring and trough-guided monitoring, though AUC-guided monitoring yielded numerically lower risks (OR 0.54; 95% CI 0.28 to 1.01). Nevertheless, the findings may be limited by the lack of high-quality randomized trials, variations in AUC calculations, and different definitions of AKI. [8]

Background References: [1] Rybak MJ, Le J, Lodise TP, et al. Therapeutic monitoring of vancomycin for serious methicillin-resistant Staphylococcus aureus infections: A revised consensus guideline and review by the American Society of Health-System Pharmacists, the Infectious Diseases Society of America, the Pediatric Infectious Diseases Society, and the Society of Infectious Diseases Pharmacists. Am J Health Syst Pharm. 2020;77(11):835-864. doi:10.1093/ajhp/zxaa036
[2] Rybak MJ, Lomaestro BM, Rotschafer JC, et al. Vancomycin therapeutic guidelines: a summary of consensus recommendations from the infectious diseases Society of America, the American Society of Health-System Pharmacists, and the Society of Infectious Diseases Pharmacists [published correction appears in Clin Infect Dis. 2009 Nov 1;49(9):1465]. Clin Infect Dis. 2009;49(3):325-327. doi:10.1086/600877
[3] Lodise TP, Drusano G. Vancomycin Area Under the Curve-Guided Dosing and Monitoring for Adult and Pediatric Patients With Suspected or Documented Serious Methicillin-Resistant Staphylococcus aureus Infections: Putting the Safety of Our Patients First. Clin Infect Dis. 2021;72(9):1497-1501. doi:10.1093/cid/ciaa1744
[4] Finch NA, Zasowski EJ, Murray KP, et al. A Quasi-Experiment To Study the Impact of Vancomycin Area under the Concentration-Time Curve-Guided Dosing on Vancomycin-Associated Nephrotoxicity. Antimicrob Agents Chemother. 2017;61(12):e01293-17. Published 2017 Nov 22. doi:10.1128/AAC.01293-17
[5] Neely MN, Kato L, Youn G, et al. Prospective Trial on the Use of Trough Concentration versus Area under the Curve To Determine Therapeutic Vancomycin Dosing. Antimicrob Agents Chemother. 2018;62(2):e02042-17. Published 2018 Jan 25. doi:10.1128/AAC.02042-17
[6] Lim AS, Foo SHW, Benjamin Seng JJ, Magdeline Ng TT, Chng HT, Han Z. Area-Under-Curve-Guided Versus Trough-Guided Monitoring of Vancomycin and Its Impact on Nephrotoxicity: A Systematic Review and Meta-Analysis. Ther Drug Monit. 2023;45(4):519-532. doi:10.1097/FTD.0000000000001075
[7] Liu SP, Xiao J, Liu YL, et al. Systematic review of efficacy, safety and pharmacokinetics of intravenous and intraventricular vancomycin for central nervous system infections. Front Pharmacol. 2022;13:1056148. Published 2022 Nov 18. doi:10.3389/fphar.2022.1056148
[8] Tsutsuura M, Moriyama H, Kojima N, et al. The monitoring of vancomycin: a systematic review and meta-analyses of area under the concentration-time curve-guided dosing and trough-guided dosing. BMC Infect Dis. 2021;21(1):153. Published 2021 Feb 6. doi:10.1186/s12879-021-05858-6
Literature Review

A search of the published medical literature revealed 4 studies investigating the researchable question:

What evidence is there to support AUC:MIC dosing of vancomycin for CNS infections?

Level of evidence

C - Multiple studies with limitations or conflicting results  Read more→



Please see Tables 1-4 for your response.


A Quasi-Experiment To Study the Impact of Vancomycin Area under the Concentration-Time Curve-Guided Dosing on Vancomycin-Associated Nephrotoxicity
Design

Single-center, retrospective quasi-experiment

N= 1,280

Objective To assess the impact of switching from trough concentration-guided dosing to AUC-guided dosing on vancomycin-associated nephrotoxicity
Study Groups

Trough concentration-guided dosing (n= 546)

AUC-guided dosing (n= 734)

Inclusion Criteria Hospitalized patients receiving intravenous vancomycin for at least 72 hours for a documented or suspected infection from January 2014 through December 2015
Exclusion Criteria Patients with a preexisting need for renal replacement therapy or a baseline serum creatinine concentration of ≥2 mg/dl; patients treated for meningitis, skin and soft tissue infections without concomitant bacteremia, urinary tract infections, or surgical prophylaxis; patients receiving concomitant piperacillin-tazobactam
Methods Comparison of nephrotoxicity incidence between AUC24 and trough concentration monitoring strategies. Multivariable logistic and Cox proportional hazards regression were used to examine the association between monitoring strategy and nephrotoxicity. Secondary analysis compared vancomycin exposures between strategies.
Duration January 2014 through December 2015
Outcome Measures

Primary: Incidence of nephrotoxicity

Secondary: Vancomycin exposures (total daily dose, AUC, and trough concentrations)

Baseline Characteristics   Trough concentration-guided dosing (n= 546) AUC-guided dosing (n= 734)
Mean age, years 59.1 ± 17.5 59.0 ± 16.5
Male 296 (54.2%) 414 (56.4%)
Median weight, kg (IQR) 67.9 (56.5-75.1) 66 (56.5-75.1)
Results   Trough concentration-guided dosing (n= 546) AUC-guided dosing (n= 734) p-value
Nephrotoxicity (2009 guideline definition) 54 (9.9%) 54 (5.4%) 0.107
Akin stage 1 or worse 106 (19.4%) 132 (18.0%) 0.515
Akin stage 2 or worse 64 (11.7%) 65 (8.9%) 0.092
Adverse Events Nephrotoxicity was observed in 8.4% of patients overall. AUC-guided dosing was associated with less frequent nephrotoxicity compared to trough concentration-guided dosing.
Study Author Conclusions AUC-guided vancomycin dosing was associated with significantly reduced nephrotoxicity compared to trough concentration-guided dosing, likely due to reduced vancomycin exposure.
Critique The study's retrospective design and single-center setting may limit generalizability. Exclusion of patients receiving concomitant piperacillin-tazobactam could introduce bias. The study did not assess the impact of AUC-guided dosing on clinical efficacy against infections.

 

Table 1 References:
[9] Finch NA, Zasowski EJ, Murray KP, et al. A Quasi-Experiment To Study the Impact of Vancomycin Area under the Concentration-Time Curve-Guided Dosing on Vancomycin-Associated Nephrotoxicity. Antimicrob Agents Chemother. 2017;61(12):e01293-17. Published 2017 Nov 22. doi:10.1128/AAC.01293-17
Prospective Trial on the Use of Trough Concentration versus Area under the Curve To Determine Therapeutic Vancomycin Dosing
Design

Prospective, serial cohort study

N= 252

Objective To test the hypothesis that AUC-guided treatment of vancomycin is more likely to be therapeutic than trough concentration-guided treatment, and to evaluate if AUC-guided dosing reduces nephrotoxicity and blood sampling without compromising efficacy
Study Groups

Year 1 (control, n= 75)

Year 2 (BestDose-MM, n= 88)

Year 3 (BestDose-MMopt, n= 89)

Inclusion Criteria Inpatients aged ≥18 years prescribed intravenous vancomycin therapy with ≥1 measured concentration, indicating continuation of therapy beyond 48 hours
Exclusion Criteria Patients on any form of renal replacement therapy and those with expected survival of less than 72 hours
Methods In year 1, nonstudy clinicians targeted trough concentrations of 10 to 20 mg/liter. In years 2 and 3, the study team used BestDose Bayesian software to achieve a daily, steady-state AUC/MIC ratio of ≥400, with a maximum AUC value of 800 mg·h/liter. Bayesian estimation of AUCs used trough samples in years 1 and 2 and optimally timed samples in year 3.
Duration December 2012 to June 2016
Outcome Measures

Primary: Proportion of therapeutic AUCs versus trough concentrations

Secondary: Nephrotoxicity, number of blood samples, length of therapy, length of hospitalization

Baseline Characteristics   Yr 1 control (n= 75) Yr 2 BestDose-MM (n= 88) Yr 3 BestDose-MMopt (n= 89)  
Mean (range) age, years 47.7 (19.0–71.0) 48.0 (18.0–93.0) 50.3 (22.0–81.0)  
No. (%) of male sex 61 (81) 67 (76) 67 (75)  
Mean (range) wt, kg 82.4 (47.7–150.9) 81.0 (46.4–193.6) 78.8 (30.3–180.0)  
Mean (range) ht, cm 171.9 (149.9–198.1) 169.1 (149.9–193.0) 168.6 (127.4–188.0)  
Results Endpoints Yr 1 control (n= 233) Yr 2 BestDose-MM (n= 189) Yr 3 BestDose-MMopt (n= 201) p-value
No. (%) of samples with concn sampled 10 to 12 h postdose ("trough") 84 (36%) 87 (46%) 43 (21%) 0.02

No. (%) of samples with indicated trough concn (mg/liter)

≤10

10 to ≤15

15 to 20

>20

 

40 (47%)

14 (17%)

22 (26%)

8 (10%)

 

61 (70%)

19 (22%)

5 (6%)

2 (2%)

 

17 (40%)

20 (46%)

4 (9%)

2 (5%)

<0.0001
Adverse Events Nephrotoxicity occurred in 8% of subjects in year 1, 0% in year 2, and 2% in year 3. Higher baseline trough concentrations and AUCs were associated with nephrotoxicity.
Study Author Conclusions AUC-guided, Bayesian estimation-assisted vancomycin dosing is more effective than trough concentration-guided dosing, reducing nephrotoxicity, blood sampling, and therapy duration without compromising efficacy, offering potential cost savings.
Critique The study's strengths include its prospective design and real-world application, demonstrating reduced nephrotoxicity and preserved efficacy with AUC-guided dosing. However, the study was not powered to evaluate efficacy for specific infections, and the diverse patient population may limit the generalizability of the findings.

 

Table 2 References:
[10] Neely MN, Kato L, Youn G, et al. Prospective Trial on the Use of Trough Concentration versus Area under the Curve To Determine Therapeutic Vancomycin Dosing. Antimicrob Agents Chemother. 2018;62(2):e02042-17. Published 2018 Jan 25. doi:10.1128/AAC.02042-17

 

A higher area under the concentration-time curve/minimum inhibitory concentration target as a potential prognostic factor for vancomycin treatment of methicillin-resistant Staphylococcus aureus meningitis: A case report

Design

Case report

Case presentation

A 61-year-old woman who underwent ventriculoperitoneal (VP) shunt placement following subarachnoid hemorrhage developed healthcare-associated meningitis due to shunt infection. Gram-positive cocci were identified by CSF Gram stain, and MRSA was confirmed by molecular testing. Targeted therapy with IV vancomycin at 25 mg/kg every 12 hours was initiated after initial treatment with piperacillin-tazobactam. Serial therapeutic drug monitoring was performed utilizing Bayesian software to estimate pharmacokinetic parameters from paired peak and trough levels. On postoperative day (POD) 24, an AUC/MIC of 515 was achieved, but CSF cultures remained positive.

Escalation of vancomycin dosing to 30 mg/kg every 8 hours increased the AUC/MIC to 610 by POD 28, with a concurrent increase in trough to 18.6 μg/mL. CSF cultures turned negative by POD 30, and an AUC/MIC of 700 was recorded. Therapeutic efficacy coincided with higher vancomycin AUC exposure, suggesting a potential benefit of targeting an AUC/MIC at or near the upper boundary of the recommended therapeutic window (400–600) in CNS infections. The vancomycin CSF-to-serum ratio averaged approximately 41%, with CSF concentrations of 5.4 μg/mL at MRSA-positive and 6.2 μg/mL at MRSA-negative culture points. Despite achieving early bloodstream clearance, CSF sterilization lagged until AUC/MIC exceeded 600, supporting the notion that the conventional target of ≥400 may be insufficient for MRSA meningitis. Notably, the patient experienced no vancomycin-associated nephrotoxicity during therapy, although a non-serious drug eruption prompted treatment discontinuation on POD 47.

Study Author Conclusions

In conclusion, the use of the AUC-guided strategy for therapeutic monitoring appears promising. If this strategy is adopted as a monitoring parameter, a higher target vancomycin AUC/MIC near the upper limit of the therapeutic window may be appropriate for MRSA meningitis. Further research is imperative to determine the ideal vancomycin AUC/ MIC and the concentrations or AUC in CSF for treating MRSA meningitis.

 

Table 3 References:
[11] Nakazono K, Saito H, Ohkubo A, et al. A higher area under the concentration-time curve/minimum inhibitory concentration target as a potential prognostic factor for vancomycin treatment of methicillin-resistant Staphylococcus aureus meningitis: A case report. IDCases. 2024;37:e02035. Published 2024 Jul 20. doi:10.1016/j.idcr.2024.e02035

Population pharmacokinetics of vancomycin in serum and cerebrospinal fluid: variability in cerebrospinal fluid concentrations despite targeted serum exposure
Design

Retrospective, single-center, open-label, observational study

N= 64

Objective To develop a population pharmacokinetic model simultaneously describing vancomycin concentrations in serum and cerebrospinal fluid (CSF) using real-world therapeutic drug monitoring (TDM) data and to characterize the relationship between systemic and CSF exposure
Study Groups All patients (N= 64)
Inclusion Criteria Adult neurosurgical patients aged ≥18 years treated with vancomycin for secondary meningitis with at least one measured serum and one CSF vancomycin concentration obtained during the initial phase of therapy (within the first 4 days of treatment)
Exclusion Criteria None specified
Methods Vancomycin concentrations were measured as part of routine TDM, and concentration in serum and CSF were analyzed using nonlinear mixed-effects modeling. Monte Carlo simulations were performed to evaluate exposure across dosing regimens and renal function strata. A two-compartment model with a CSF compartment was used. Clearance was associated with the estimated glomerular filtration rate. Simulations under targeted serum exposure (area under the curve, AUC24 ~500 mg·h/L) were used to isolate variability in CSF exposure.
Duration January 2017 to January 2026
Outcome Measures

Primary: Development of a population pharmacokinetic model

Secondary: Characterization of the relationship between serum and CSF exposure, quantification of variability in CSF drug concentrations

Baseline Characteristics  

All patients

(N= 64)

Sex M/F, n (%) 36 (56.2)/28 (44.8)
Median age, years (IQR) [range] 55 (45–67.5) [18–82]
Height, cm (IQR) [range] 175 (167–180) [154–197]
Body weight, kg (IQR) [range] 85 (70–95) [48–140]
Ideal body weight, kg (IQR) [range] 66 (58–75) [47–87]
Adjusted body weight, kg (IQR) [range] 75 (65–82) [48–100]
Lean body mass, kg (IQR) [range] 57 (49–65) [35–80]
Body surface area, m2 (IQR) [range] 2.03 (1.85–2.18) [1.51–2.62]
Body mass index, kg/m2 (IQR) [range] 26.5 (24.1–31.2) [16.6–46.2]
Serum creatinine, µmol/L (IQR) [range] 61 (50–74) [23–124]
eGFRnorm, mL/min/1.73 m(IQR) [range] 106.5 (90.5–119.0) [53.4–138]
eGFR, mL/min (IQR) [range] 119.8 (101.0–136.0) [56.2–185.5]
Coefficient of energy balance (IQR) [range] 1.05 (−57.4 to 17.4) [−2,259.5 to 31.5]
CSF albumin, g/L (IQR) [range] 0.8 (0.4–1.1) [0–16.6]
CSF total protein, g/L (IQR) [range] 1.39 (0.77–1.99) [0.09–28.94]
Polymorphonuclear leukocytes in CSF, cells/mcL (IQR) [range] 122.5 (26.5–937.5) [0–22,199]
Results   Estimate Relative standard error (%) Bootstrap analysis, median (2.5th–97.5th percentile)
Vd_pop (L) 115.1 10.7 108.3 (84.9–133.8)
CL_pop (L/h) 6.50 4.61 6.49 (5.94–7.09)
CLCSF_pop (L/h) 0.019 13.8 0.015 (0.007–0.039)
ωVd 41.0 19.5 40.0 (21.0–58.0)
ωCL 30.0 11.4 29.0 (22.0–36.0)
ωQ 31.0 43.9 40.0 (16.0–60.0)
ωCLCSF 42.0 22.4 36.0 (17.0–61.0)
Error model parameters- Proportional (serum) 0.15 10.7 0.14 (0.11–0.19)
Error model parameters-Proportional (CSF) 0.16 18.4 0.15 (0.073–0.22)
Adverse Events N/A
Study Author Conclusions Vancomycin CSF exposure exhibits substantial variability that is not reliably predicted by serum pharmacokinetics, even under standardized systemic exposure. These findings highlight limitations of serum-guided dosing for CNS infections and support the need for compartment-specific dosing strategies and PK/PD targets.
Critique The study provides a comprehensive analysis of vancomycin pharmacokinetics in serum and CSF, highlighting the variability in CSF exposure. However, the retrospective design and reliance on routine TDM data may limit the precision of parameter estimates. The study's findings are primarily applicable to patients with secondary post-neurosurgical meningitis, and the lack of linked microbiological and clinical outcome data limits the assessment of exposure-response relationships. Additionally, the absence of an external validation cohort restricts the evaluation of the model's predictive performance in independent populations. Even when serum AUC was tightly targeted around 500 mg·h/L, CSF concentrations remained highly variable, concluding that serum-guided AUC targets don't reliably predict CNS drug exposure and that compartment-specific PK/PD targets are needed.
Table 4 References:
[12] Polkov L, Moravec T, Krej V, et al. Population pharmacokinetics of vancomycin in serum and cerebrospinal fluid: variability in cerebrospinal fluid concentrations despite targeted serum exposure. Antimicrob Agents Chemother. 2026 Jun 15:e0056926. doi:10.1128/aac.00569-26